An open label extension shows additional benefit from a drug currently being tested for patients with Lou Gehrig’s disease.

A computer simulation reveals the metabolic dysfunction behind heart failure.

Percentage of all child health spending that went to orphan drugs rose 65% in five years, while families’ portion rose even faster.

Researchers explore the relationship between the Centers for Medicare and Medicaid Services financial incentives and hospital participation in a voluntary advanced alternative payment program.

A new observational study finds patients in the hospital for COVID-19 have high levels of soluble urokinase receptor (suPAR), an immune-derived pathogenic protein that is strongly predictive of kidney injury.

Researchers report first clinically actionable findings for a rare blood vessel disease in a study of four unrelated families, all with the same genetic variant.